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Updated: Jul 20, 2025

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作为帕金森病治疗工具的CRISPR/sgRNA导向协同激活介质 (SAM)

Luis Fernando Narváez-Pérez1, Francisco Paz-Bermúdez1, José Arturo Avalos-Fuentes1

  • 1Departamento de Fisiología, Biofísica y Neurociencias, Centro de Investigación y de Estudios Avanzados del Instituto Politécnico Nacional, Ciudad de México, 07360, México.

Gene therapy
|August 4, 2023
PubMed
概括

这项研究证明了使用CRISPR来使星球细胞产生多巴胺的帕金森病新型基因疗法. 这种方法成功地改善了大鼠模型中的运动功能.

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