预防规则:一个评估罕见疾病预防干预措施的潜在框架
Eddie Gibson1, Daniel A Ollendorf2, Steven Simoens3
1Wickenstones Ltd, Abingdon, UK.
Journal of market access & health policy
|August 16, 2023
概括
标准卫生技术评估 (HTA) 需要修改,以评估罕见疾病预防. 提出一个建议.
科学领域:
- 医疗技术评估 (HTA) 是指对医疗技术进行评估.
- 公共卫生政策 公共卫生政策
- 罕见和传染性疾病.
背景情况:
- 标准卫生技术评估 (HTA) 往往缺乏对预防干预措施的全面评估,特别是在罕见和传染性疾病方面.
- 现有的HTA框架可能无法完全捕捉到疾病预防与治疗的独特价值主张.
研究的目的:
- 通过在罕见疾病治疗和预防之间进行并行分析,探索未来HTA的考虑因素.
- 评估当前HTA框架对罕见,传染性和可预防疾病的适用性.
- 确定必要的修改,以将预防特异性价值元素纳入HTA.
主要方法:
- 召集专家小组,评估单一HTA框架对于罕见疾病治疗和预防干预措施的适应性.
- 评估了当前HTA中的价值元素的范围及其与罕见,传染性和可预防疾病的相关性.
主要成果:
- 为了评估罕见的传染性疾病的预防,需要综合考虑各种价值因素.
- 虽然标准的HTA可以解决传染性疾病,但对于大规模的预防计划,需要修改框架,考虑到疫情风险.
- 提出了一个"预防规则"框架,将严重性,公平性和预防益处纳入罕见传染病干预措施的决策.
结论:
- 拟议的"预防规则"框架提供了一种结构化的方法,用于一致评估罕见传染病.
- 该框架明确纳入了预防性干预的更广泛价值,比以治疗为重点的评估提供了明显的优势.
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