Ruta Brazauskas1, Mary Eapen2, Tao Wang1

  • 1Division of Biostatistics, Institute for Health and Equity, Medical College of Wisconsin, 8701 Watertown Plank Road, Milwaukee, WI, 53226, USA.

概括

本综述详细介绍了血液病研究的常见结果和终点,强调了治疗安全性和疗效的临床结果. 它还强调了患者报告的结果,并为在临床试验中选择初级和二级终点提供了指导.