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Updated: Jul 18, 2025

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恢复纤维功能:用于原发性纤维功能障碍的基因治疗方法

Nicholas W Keiser1, Erin Cant2, Sneha Sitaraman1

  • 1Spirovant Sciences, Inc., Philadelphia, Pennsylvania, USA.

Human gene therapy
|August 25, 2023
PubMed
概括

初级状动力障碍 (PCD) 是一种影响动的遗传疾病,导致肺部疾病. 基因疗法为这种复杂的疾病提供了有前途的未来治疗方法.

关键词:
在 AAV AAV AAV 中.西里亚西里亚是什么意思基因治疗的基因疗法肺 肺 肺 肺 肺 肺 肺 肺 肺病毒载体病毒载体

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