最近在CRISPR/Cas9传递方法中的进展,用于干细胞的治疗基因编辑

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Updated: Jul 16, 2025

CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications
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CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications

Published on: August 9, 2022

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Malihe Lotfi1,2,3, Dorsa Morshedi Rad4, Samaneh Sharif Mashhadi2,3

  • 1Student Research Committee, Faculty of Medicine, Mashhad University of Medical Sciences, Mashhad, Iran.

Stem cell reviews and reports
|September 18, 2023
PubMed
概括

使用CRISPR/Cas9的基因组编辑为治疗遗传疾病提供了新的希望. 本综述探讨了CRISPR/Cas9的有效输送策略,将其转化为难以转化的人类多能干细胞,用于治疗应用.

关键词:
这是一个CRISPR/Cas9系统.交付技术提供技术.基因编辑 基因编辑干细胞疗法是一种干细胞疗法.干细胞是一种干细胞.

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