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对于治疗和管理米加拉斯塔特的法布里病患者的共识建议:修改后的Delphi研究

Daniel G Bichet1, Robert J Hopkin2, Patrício Aguiar3,4

  • 1Department of Medicine, Pharmacology and Physiology, Hôpital du Sacré-Coeur, University of Montréal, Montreal, QC, Canada.

Frontiers in medicine
|September 20, 2023
PubMed
概括

对于在法布里病中治疗米加拉斯塔的共识建议强调整体的,多学科的护理. 专家们一致同意使用米加拉斯塔特 (migalastat) 的指导方针,这是一种陪伴者治疗,并监测患有法布里病的患者.

关键词:
阿尔法-银酸酶A的作用.适应性 适应性 适应性陪伴者治疗是一种陪伴疗法.全球三氧化三氧化三氧化三氧化患者的旅程 患者的旅程治疗决策 治疗决策

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