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Updated: Jul 16, 2025

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在特殊人群中使用CFTR调节剂,第2部分:严重肺部疾病

Joseph Elijah1,2,3, Linda J Fitzgerald1,2,4, Hanna Phan1,2,5

  • 1Department of Pharmacy Services, Michigan Medicine, Ann Arbor, Michigan Medicine, USA.

Pediatric pulmonology
|September 20, 2023
PubMed
概括

囊性纤维化跨膜调节器 (CFTR) 调节器对严重肺病患者显示出显著的益处. 虽然通常是安全的,但谨慎的剂量和监测是关键,特别是对于儿科患者.

关键词:
在CFTR调节器.囊性纤维化症是什么严重的肺部疾病.

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