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Updated: Jul 15, 2025

Forskolin-induced Swelling in Intestinal Organoids: An In Vitro Assay for Assessing Drug Response in Cystic Fibrosis Patients
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囊性纤维化药物开发管道的进展

Christine Esposito1, Martin Kamper1, Jessica Trentacoste1

  • 1Division of Pulmonary, Critical Care and Sleep Medicine, Donald and Barbara Zucker School of Medicine at Hofstra/Northwell, New Hyde Park, New York, NY 11042, USA.

Life (Basel, Switzerland)
|September 28, 2023
PubMed
概括

囊性纤维化治疗正在进步,改善了患者的生活质量和生存率. 包括遗传方法在内的新疗法旨在为这种进展性遗传疾病提供治疗方法.

关键词:
这是一种抗炎药物.抗生素 抗生素是一种抗生素.细菌菌体是一种菌体.囊性纤维化 (CF)囊性纤维化转膜导电调节器 (CFTR)基因疗法是基于基因的疗法.高效的调节器疗法 (HEMT)粘菌解毒疗法 粘菌解毒疗法

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