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Updated: Jul 13, 2025

Real-Time Fluorescent Measurement of Synaptic Functions in Models of Amyotrophic Lateral Sclerosis
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关于C9ORF72前性痴呆症和骨髓缩侧面硬化症的路线图:关于C9ORF72FTD/ALS峰会的报告

Rita Sattler1, Bryan J Traynor2, Janice Robertson3

  • 1Barrow Neurological Institute, 2910 N Third Ave, Phoenix, AZ, 85013, USA. rita.sattler@barrowneuro.org.

Neurology and therapy
|October 17, 2023
PubMed
概括

一次峰会召集专家讨论C9ORF72基因扩张,这是前性痴呆症 (FTD) 和肌缩侧面硬化症 (ALS) 的关键因素. 合作努力和新的治疗策略对于推进C9ORF72-FTD/ALS治疗和临床试验至关重要.

关键词:
生物标志物生物标志物C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C9ORF72C双重复蛋白质重复蛋白质是什么基因治疗是一种基因疗法.神经纤维纤维是一种神经纤维.预防 预防 预防在RNA中毒性RNA毒性在TDP-43中使用.

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