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Updated: Jul 11, 2025

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普拉德-威利综合征患者的二氧化胆延长释放片:从长期开放标签研究的结果

Jennifer L Miller1, Evelien Gevers2, Nicola Bridges3

  • 1Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, USA.

Obesity (Silver Spring, Md.)
|November 3, 2023
PubMed
概括

氧化胆延长释放 (DCCR) 显著改善了普拉德-威利综合征 (PWS) 的过和行为症状. 这种治疗有可能减少PWS患者和家属的疾病严重程度和护理负担.

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