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努辛森治疗脊柱肌肉缩I型与慢性呼吸衰竭:韩国的一项回顾性研究

Hui Jin Shin1, Ji-Hoon Na1, Hyunjoo Lee1

  • 1Department of Pediatrics, Gangnam Severance Hospital, Severance Children's Hospital, Yonsei University College of Medicine, Seoul, Korea.

Yonsei medical journal
|November 22, 2023
PubMed
概括

努辛森在治疗I型脊髓肌缩症 (SMA) 中证明了安全性和有效性,即使是在需要永久通风的慢性呼吸衰竭患者中也是如此. 治疗显示了运动功能得分和疾病改善的显著改善.

关键词:
韩国 韩国 韩国 韩国脊柱肌肉缩 脊柱肌肉缩 脊柱肌肉缩机动功能 机动功能 机动功能没有任何的 nusinersenersen.呼吸衰竭是指呼吸系统的衰竭.

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