中枢神经系统炎症作为补充因子I缺乏的第一个迹象:一种严重的髓炎,用强化免疫疗法和eculizumab治疗

Valérie Massey1, Cam-Tu Emilie Nguyen1, Tine François1

  • 1From the Immunology and Rheumatology Division (V.M., J.J.D.B., H.D.), Department of Pediatrics, Sainte-Justine University Hospital Center; Allergy and Immunology Division (V.M.), Sacré-Coeur Hospital; Neurology Division (C.-T.E.N.), Department of Pediatrics; Intensive Care Division (T.F., A.B.), Department of Pediatrics; Clinical Department of Laboratory Medicine (A.B.), OPTILAB; and Nephrology Division (A.-L.L.), Department of Pediatrics, Sainte-Justine University Hospital Center, Montreal, Canada.

概括

完全补充因子I (CFI) 缺乏可以导致严重的中枢神经系统 (CNS) 炎症作为最初的症状. 快速补充阻塞疗法,如eculizumab,对于控制急性炎症和预防复发至关重要.