,

Huseyin O Taskin1, Jacqueline Wivel2, Gustavo D Aguirre2

  • 1Department of Neurology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA 19104.

概括

狗的功能性MRI评估形视力恢复遗传性视网膜疾病. NPHP5-CRD2模型对旨在恢复形功能的基因疗法研究具有前景.

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