[对神经纤维素瘤类型1的基因治疗策略和前景]

Tingting Zheng1,2, Beiyao Zhu1,2, Zhichao Wang1,2

  • 1Department of Plastic and Reconstructive Surgery, Shanghai Ninth People's Hospital, Shanghai Jiao Tong University School of Medicine, Shanghai, 200011, P. R. China.

概括

基因疗法为神经纤维素炎1型 (NF1) 提供了有前途的新治疗途径. 研究正在为这种遗传性疾病推进转基因疗法和基因编辑.