相关实验视频

Updated: Jul 1, 2025

Subconjunctival Administration of Adeno-associated Virus Vectors in Small Animal Models
06:16

Subconjunctival Administration of Adeno-associated Virus Vectors in Small Animal Models

Published on: March 16, 2022

2.9K

临床药理学对开发腺相关病毒载体基视网膜基因治疗的观点

Jennifer Lynn Ford1, Eleni Karatza1, Hardik Mody1

  • 1Janssen Research & Development, LLC, Spring House, Pennsylvania, USA.

Clinical pharmacology and therapeutics
|March 7, 2024
PubMed
概括

基因相关病毒 (AAV) 基因疗法为治疗眼睛疾病提供了一种有前途的方法,这是由于眼睛的可访问性和免疫特权. 本综述综合了推动基于AAV的视网膜基因治疗从临床前研究到临床应用的关键考虑因素.

更多相关视频

Limbal Approach-Subretinal Injection of Viral Vectors for Gene Therapy in Mice Retinal Pigment Epithelium06:48

Limbal Approach-Subretinal Injection of Viral Vectors for Gene Therapy in Mice Retinal Pigment Epithelium

Published on: August 7, 2015

21.3K
Author Spotlight: Addressing Regulatory Gaps in Molecular Studies by Quantifying Viral Vectors in Complex Matrices07:43

Author Spotlight: Addressing Regulatory Gaps in Molecular Studies by Quantifying Viral Vectors in Complex Matrices

Published on: July 14, 2023

1.9K

相关概念视频

Gene Therapy00:59

Gene Therapy

Gene therapy is a technique where a gene is inserted into a person’s cells to prevent or treat a serious disease. The added gene may be a healthy version of the gene that is mutated in the patient, or it could be a different gene that inactivates or compensates for the patient’s disease-causing gene. For example, in patients with severe combined immunodeficiency (SCID) due to a mutation in the gene for the enzyme adenosine deaminase, a functioning version of the gene can be...
25.4K