随机平台试验的特征,进展和结果:系统性审查
Alexandra Griessbach1, Christof Manuel Schönenberger1, Ala Taji Heravi1
1CLEAR Methods Center, Division of Clinical Epidemiology, Department of Clinical Research, University Hospital Basel, University of Basel, Basel, Switzerland.
JAMA network open
|March 20, 2024
概括
随机平台试验在COVID-19期间激增,但自那以后已经下降. 报告试验特征和结果是不够的,尽管过早关闭手臂是罕见的.
科学领域:
- 临床试验的设计
- 流行病学 流行病学
- 生物统计学 生物统计学
背景情况:
- 平台试验在临床研究中越来越多地被使用.
- 需要证据证明它们的实际应用,特征,进展和输出.
结论:
- 在COVID-19大流行期间,平台试验活动激增,但此后已经下降.
- 观察到平台试验特征的报告不足,结果的可用性有限.
- 尽管面临挑战,但由于招募问题而过早关闭武器是罕见的.
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