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开发和描述一流的可调剂量基因疗法系统

Alex Goraltchouk1, Jared Lourie2, Judith M Hollander1

  • 1Remedium Bio, Inc. 1116 Great Plain Ave, Suite 203, Needham, MA 02492, United States of America.

Gene
|April 25, 2024
PubMed
概括

这项研究引入了一种使用脂质纳米粒子 (LNP) 的新型可调剂量基因疗法. 该平台为蛋白质替代提供了低成本,单次注射的解决方案,克服了当前基因疗法的局限性.

关键词:
剂量调整剂量调整基因治疗是一种基因疗法.脂质纳米颗粒的使用方法非病毒性传递非病毒性传递在皮下进行皮下注射.

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