项目SATURN-一个现实世界的证据数据与Osteogenesis Imperfecta的现有欧洲数据集的合作,以支持未来的疗法
L Sangiorgi1, M Boarini1, I Westerheim2
1Department of Rare Skeletal Disorders, IRCCS Istituto Ortopedico Rizzoli, Bologna, Italy.
Orphanet journal of rare diseases
|May 2, 2024
概括
项目SATURN旨在通过创建一个统一的数据集来简化患者获得新的罕见病疗法. 这项针对骨质发育不完美的倡议可以加速全球患者的药物可用性.
科学领域:
- 药物经济学和卫生技术评估
- 罕见疾病研究 罕见疾病研究
- 现实世界的证据生成
关键词:
一个共同的核心数据集.卫生技术评估 卫生技术评估医疗保健系统 医疗保健系统自然历史,自然历史.骨质发生不完美 (osteogenesis imperfecta) 是一个不完美的疾病.罕见的疾病 罕见的疾病现实世界的数据数据.登记处 登记处 登记处 登记处监管机构 监管机构更多相关视频
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