Mariam Barak1, Christopher Hu1, Alicia Matthews1

  • 1Biology Department, Case Western Reserve University, Cleveland, OH 44106, USA.

Cells
|May 24, 2024
PubMed
概括

新的基因疗法为状细胞疾病 (SCD) 提供了潜在的治疗方法,但正在进行的研究对于了解长期影响和为这种常见的遗传性血液疾病开发更容易获得的治疗方法至关重要.

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