实地研究和对因子IX变异FIX-R338L的相关研究在参与者治疗费达纳古elaparvovec治疗

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Measurement of Factor V Activity in Human Plasma Using a Microplate Coagulation Assay
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Measurement of Factor V Activity in Human Plasma Using a Microplate Coagulation Assay

Published on: September 9, 2012

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Debra D Pittman1, Charles Carrieri2, Holly Soares2

  • 1Rare Disease Research Unit, Pfizer Inc., Cambridge, Massachusetts, United States.

Thrombosis and haemostasis
|June 12, 2024
PubMed
概括

在B型血友病基因治疗中测量因子IX-R338L活性的试验显示出变异性,特别是在低水平. 优化试验选择对于准确评估费达纳科根elaparvovec治疗疗效至关重要.

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