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Updated: Jun 22, 2025

Lentiviral Vector Platform for the Efficient Delivery of Epigenome-editing Tools into Human Induced Pluripotent Stem Cell-derived Disease Models
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精确的行动:在基因疗法中集群定期间隔的短时间的Palindromic重复/案例的作用

Amrutha Banda1, Olivia Impomeni1, Aparana Singh2

  • 1Department of Biology, The College of New Jersey, Ewing Township, NJ 08618, USA.

Vaccines
|June 27, 2024
PubMed
概括

聚类正规间隔短时间的Palindromic重复 (CRISPR) 相关酶 (Cas) 基因编辑显示出治疗疾病的前景. 开发有效的传递系统是克服挑战的关键,例如非目标效应和免疫反应,以获得安全和精确的疗法.

关键词:
这就是CRISPR/CasPR.癌症 癌症 癌症 癌症 癌症基因传递 基因传递 基因传递基因治疗的基因疗法遗传病是一种遗传性疾病.基因组编辑 基因组编辑感染的感染感染.病毒载体病毒载体

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