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在米加拉斯塔特上增强法布里病酶研究:费用费用

Mathura Kugan1, Simona D'Amore1, Udita Mitra-Royhurst1

  • 1Lysosomal Storage Disorders Unit, Royal Free Hospital NHS Foundation Trust London, United Kingdom.

Clinica chimica acta; international journal of clinical chemistry
|July 4, 2024
PubMed
概括

这项研究表明,米格拉拉斯塔特可增强法-银酸酶A活性在法布里病患者中. 白细胞α-galactosidase A的增加,和lys-Gb3水平的相关性很好,支持干血斑点的监测实用性.

关键词:
酶替代疗法是一种酶替代疗法.费布里病是什么意思 费布里病是什么意思米加拉斯塔特州这就是lyso-Gb3的原因.α-Galactosidase A 活性的一种活动.

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