TaqTth-hpRNA:RNA,mRNA

Chong Xu1,2, Jiyanuo Cao1, Huanran Qiang1

  • 1School of Basic Medical Science and Clinical Pharmacy, China Pharmaceutical University, Nanjing, 210009, China.

Genome biology
|July 7, 2024
PubMed
概括

我们开发了一种新的RNA分裂工具,TaqTth-hpRNA,用于基因治疗. 这种工具在阿尔茨海默病模型中有效地使引起疾病的突变APPmRNA沉默,显示出对遗传疾病的治疗潜力.

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