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Updated: May 11, 2026

Measurements of Motor Function and Other Clinical Outcome Parameters in Ambulant Children with Duchenne Muscular Dystrophy
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荷兰 Dystrophinopathy 数据库:一个国家注册表,标准化的患者和临床医生报告了真实世界的数据

N M van de Velde1,2, Y D Krom1,2, J Bongers1,2

  • 1Department of Neurology, Leiden University Medical Center, Leiden, The Netherlands.

Journal of neuromuscular diseases
|July 20, 2024
PubMed
概括

荷兰肌肉发育不良症数据库 (DDD) 是一个新的肌肉发育不良症患者的国家注册表. 它收集高质量的数据,以加快杜恩和贝克尔肌肉发育不良的治疗开发和研究.

关键词:
贝克尔肌肉缩症 贝克尔肌肉缩症杜申尼肌肉发育不良症是什么这是公平的,公平的.现实世界的数据.登记处的注册表可以看到.试验准备 试验准备

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