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Updated: Jun 18, 2025

Using Reference Reagents to Confirm Robustness of Cytokine Release Assays for the Prediction of Monoclonal Antibody Safety
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卡斯格维:创新药品需要对监管评估采取创新方法

Essam Kerwash1, John D Johnston1

  • 1Medicines and Healthcare Products Regulatory Agency (MHRA), 10 South Colonnade, Canary Wharf, London E14 4PU, UK.

Pharmaceutics
|July 27, 2024
PubMed
概括

基因编辑疗法Casgevy (exa-cel) 显示,在依赖输血的β-血病患者中,消除红细胞输血的概率为93%. 长期的安全性和有效性耐用性需要进一步研究.

关键词:
在CRISPR-Cas9中介的基因编辑技术中.卡斯格维·卡斯格维·卡斯格维是什么意思图尔明计划 图尔明计划分析因果影响的原因分析.输血依赖的β-thalassemia是输血依赖的

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