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腺相关病毒载体基因疗法:儿童肝病学家面临的挑战

Barath Jagadisan1, Anil Dhawan1

  • 1Paediatric Liver GI and Nutrition Centre and Mowat Labs, King's College Hospital, London, UK.

Journal of pediatric gastroenterology and nutrition
|July 29, 2024
PubMed
概括

腺相关病毒基因疗法的肝毒性正在上升. 需要更多的研究来制定有效的管理方案,并了解长期肝损伤风险.

关键词:
肝毒性 肝毒性 肝毒性基酸莫菲蒂尔是什么这是西洛利斯 ( sirolimus).类固醇类固醇是什么这就是塔克罗利斯.

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