在状细胞疾病中,PGC-1α激素诱导胎儿血红蛋白并产生抗效应

Yanan Sun1, Hajar Benmhammed1, Salam Al Abdullatif2

  • 1Section of Hematology-Medical Oncology, Department of Medicine, Boston Medical Center, Boston University Chobanian & Avedisian School of Medicine, Boston, MA, USA.

Science advances
|July 31, 2024
PubMed
概括

一种新药,SR-18292,可以提高状细胞病患者的胎儿血红蛋白. 这种方法显著减少了状红细胞,并减轻了疾病并发症,提供了一个有前途的新疗法.

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