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Updated: Jul 29, 2026

Intracranial Injection of Adeno-associated Viral Vectors
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腺相关的病毒载体集成:对长期疗效和安全性的影响

Paul Batty1, David Lillicrap2

  • 1Department of Haematology, Cancer Institute, University College London, London, United Kingdom; Department of Pathology and Molecular Medicine, Queen's University, Kingston, Ontario, Canada.

Journal of thrombosis and haemostasis : JTH
|August 3, 2024
PubMed
概括

基因相关病毒 (AAV) 基因疗法对遗传性疾病显示出有前途. 本综述研究了AAV载体的持久性,重点关注基因组整合及其对患者的长期安全影响.

关键词:
腺相关病毒的病毒.一个剧集的情节.基因治疗的基因疗法血友病A型 血友病A型 血友病A型病毒整合 病毒整合

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