视网膜益生素异型PRLΔE1在遗传性视网膜退行症中维持病

Raghavi Sudharsan1, Jennifer Kwok2, Malgorzata Swider3

  • 1Division of Experimental Retinal Therapies, Department of Clinical Sciences & Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA, USA. raghavi@vet.upenn.edu.

Cell death & disease
|September 18, 2024
PubMed
概括

益生菌异型PRLΔE1驱动了继承性视网膜退化中缓慢的光感受细胞损失. 基因疗法抑制PRLΔE1,但需要进一步研究以获得安全,有针对性的干预措施.