Taha Qarni1, Orly Moshe-Lilie2, Michelle C Kaku3

  • 1Department of Neurology, University of Pennsylvania, Philadelphia, Pennsylvania.

Seminars in neurology
|October 15, 2024
PubMed
概括

遗传性转基因氨基粉症 (ATTRv) 的诊断和治疗在新的成像和疗法方面取得了重大进展. 目前正在进行的研究解决了诸如早期检测和管理复杂的表型等挑战,以改善患者的治疗结果.

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