用Efanesoctocog Alfa治疗严重血友病A的患者经验:从XTEND-1临床研究3期出口访谈中得出的结果

Dana DiBenedetti1, Daniela Neme2, Brigitte Pan-Petesch3

  • 1RTI Health Solutions, Research Triangle Park, North Carolina.

Clinical therapeutics
|October 16, 2024
PubMed
概括

每周一次的efanesoctocog alfa预防治疗显著改善了严重血友病A患者的疼痛和身体功能,大多数人更喜欢它而不是以前的治疗方法. 这与定量研究的结果一致.

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