Voxelotor

Gonzalo De Luna1, Anoosha Habibi1, Stéphane Moutereau2

  • 1Sickle Cell Referral Center, Department of Internal Medicine, Henri-Mondor University Hospital- UPEC, Créteil, France.

PubMed
概括

在状细胞病患者的Voxelotor治疗导致6个月后胎儿血红蛋白 (HbF) 水平下降. 这一发现引发了人们对Voxelotor因其短半衰期而停止使用后潜在的反弹效应的担忧.

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