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Updated: Jun 9, 2025

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重新思考用于肌缩侧面硬化症的反感寡核酸治疗方法

Daisuke Ito1,2, Kensuke Okada2

  • 1Memory Center, Keio University School of Medicine, Tokyo, Japan.

Annals of clinical and translational neurology
|October 30, 2024
PubMed
概括

反感性寡核酸对蛋白质病变,如肌缩性侧面硬化症 (ALS) 的治疗有前途. 然而,临床试验表明目标参与但没有临床益处,需要进一步研究治疗疗效.

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