AAV:

Liyan Zhang1, Fangzhi Tan1, Jieyu Qi1,2,3

  • 1State Key Laboratory of Digital Medical Engineering, Department of Otolaryngology Head and Neck Surgery, Zhongda Hospital, School of Life Sciences and Technology, School of Medicine, Advanced Institute for Life and Health, Jiangsu Province High-Tech Key Laboratory for Bio-Medical Research, Southeast University, Nanjing, 210096, China.

概括

基因疗法为遗传性聋提供了一个有前途的新疗法,成功地恢复了小鼠模型和一些患者的听力. 由于内耳的复杂性和基因多样性,需要精确的方法.