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Updated: Jun 13, 2025

A Clinical Trial Assessing the Safety, Efficacy, and Delivery of Olive-Oil-Based Three-Chamber Bags for Parenteral Nutrition
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患者报告的结果和措施在针对孤儿疾病的先进治疗药物试验中未得到充分利用

Andrada Ciuca1, Siddharth Banka2, Tara Clancy2

  • 1Department of Psychology, Babeș-Bolyai University, Cluj-Napoca, Romania.

Journal of clinical epidemiology
|November 28, 2024
PubMed
概括

很少有孤儿先进治疗药物 (ATMP) 试验使用患者报告的结果 (PRO) 和患者报告的结果措施 (PROM). 本次审查强调了需要更好的PRO/PROM整合,以捕捉罕见病研究中的患者经验.

关键词:
先进疗法的药物,先进疗法的药物.这些是PROMs.在这个过程中,PROs PROs.患者报告的结果衡量结果.患者报告的结果.罕见疾病是一种罕见的疾病.

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