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Updated: Jun 6, 2025

Functional Reconstitution and Channel Activity Measurements of Purified Wildtype and Mutant CFTR Protein
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Functional Reconstitution and Channel Activity Measurements of Purified Wildtype and Mutant CFTR Protein

Published on: March 9, 2015

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通过临床前和批准的调制剂对G85E CFTR变异进行药理救援

Valeria Tomati1, Valeria Capurro1, Emanuela Pesce1

  • 1UOC Genetica Medica, IRCCS Istituto Giannina Gaslini, Genova, Italy.

Frontiers in pharmacology
|December 3, 2024
PubMed
概括

新型药物组合有望改善囊性纤维化 (CF) G85E变异治疗. 带有ARN23765的elexacaftor比目前的疗法提供了更大的CFTR功能救援.

关键词:
在CFTR中,CFTR是最重要的.校正器 校正器 校正器 校正器门 门 门 门 这是什么意思模块化器是一个模块化器.鼻子 鼻子 鼻子这就是类型化.

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