L A de Ligt1,2,3, A E Gaartman1,2, K Konté2

  • 1Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory, Amsterdam, the Netherlands.

PubMed
概括

状细胞疾病 (SCD) 涉及改变的炎症和血管原蛋白. 像voxelotor和干细胞移植这样的治疗有助于恢复蛋白质水平,使其接近健康对照组,这表明了新的治疗点.