Gustavo D Aguirre1, William A Beltran2

  • 1Division of Experimental Retinal Therapies, Department of Clinical Sciences, University of Pennsylvania, School of Veterinary Medicine, Philadelphia, PA, 19104, USA. gda@vet.upenn.edu.

Eye (London, England)
|January 8, 2025
PubMed
概括

狗BEST1疾病模型显示RPE-光受体接口问题类似于人类BEST Vitelliform黄斑发育不良 (BVMD). 基因疗法成功地纠正了狗的视网膜病变,验证了该模型用于BVMD疗法开发.