测试从囊性纤维化患者衍生的iPSCs中分化的组织中对治疗的器官特异性反应

Abdelkader Daoud1, Sunny Xia2, Onofrio Laselva3

  • 1Programme in Molecular Medicine, Research Institute for SickKids Hospital, Toronto, Canada.

Stem cell research
|January 10, 2025
PubMed
概括

这项研究比较了囊性纤维化跨膜导电调节器 (CFTR) 调节器在患者衍生的结肠和呼吸道细胞中的有效性. 它建立了一种评估不同器官个性化CFTR疗法的方法.

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