全球对罕见病和孤儿药物定义的洞察力:一个系统的文献审查

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Updated: May 30, 2025

Drug Repurposing Hypothesis Generation Using the "RE:fine Drugs" System
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Drug Repurposing Hypothesis Generation Using the "RE:fine Drugs" System

Published on: December 11, 2016

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Ghada Mohammed Abozaid1,2, Katie Kerr3, Hiba Alomary4

  • 1Centre for Public Health, Institute of Clinical Sciences B, Royal Victoria Hospital, Queen's University Belfast School of Medicine, Dentistry and Biomedical Sciences, Belfast, UK gabozaid01@qub.ac.uk.

BMJ open
|January 25, 2025
PubMed
概括

罕见疾病 (RD) 和孤儿药物 (OD) 的全球定义缺乏一致性. 需要具体的国家标准来改善医疗保健的公平性,获得治疗和罕见病患者的治疗结果.

关键词:
流行病学研究 流行病学研究这是遗传学.卫生政策 卫生政策公共卫生 公共卫生审查 审查 审查 审查系统审查是系统的审查.

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