A-to-IRNA

Xilei Ai1, Zhuo Tang2

  • 1Natural Products Research Center, Chengdu Institute of Biology, Chinese Academy of Science, Chengdu, P.R. China; Academy of Chinese Medical Sciences, Henan University of Chinese Medicine, Zhengzhou, P.R. China.

Methods in enzymology
|January 27, 2025
PubMed
概括

RNA编辑提供了一个可逆的治疗方法,纠正突变而没有永久的基因组变化. 这项研究引入了一种新的小分子控制系统,用于使用aptazymes和ADAR酶精确编辑RNA.

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