肝脏伦病毒载体转导的分析:对临床前研究和临床基因治疗方案的含义

Peirong Hu1, Yajing Hao2, Wei Tang1

  • 1Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.

Viruses
|February 26, 2025
PubMed
概括

宿主基因变异显著影响着lentiviral基因治疗的结果. 这项研究揭示了小鼠的多样性反应,突出了个性化基因疗法和病毒载体沉默研究的潜力.

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