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Updated: May 24, 2025

Exploring Sequence Space to Identify Binding Sites for Regulatory RNA-Binding Proteins
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使用阿普坦为RNA疗法的向输送使用阿普坦

Julia Driscoll1, Piyush Gondaliya1, Dylan A Zinn1

  • 1Department of Transplantation, Mayo Clinic, Jacksonville, FL, USA.

Molecular therapy : the journal of the American Society of Gene Therapy
|March 6, 2025
PubMed
概括

能识别细胞表面分子的aptamers可以改善RNA治疗药物的向目标细胞的传递. 这种方法增强了新型基因沉默,引入或恢复疗法的临床翻译.

关键词:
对于RNA疗法来说,它是非常重要的.一个aptamer的功能化.亚胺-寡核酸奇默体生物学上的纳米微粒.合成纳米颗粒的制造

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