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在AAV介导的活体基因疗法的进展及其在中枢神经系统疾病中的应用

Shuming Wang1,2, Lin Xiao1,2

  • 1Institute for Brain Research and Rehabilitation, Guangdong Key Laboratory of Mental Health and Cognitive Science, Center for Studies of Psychological Application, South China Normal University, Guangzhou 510631, China.

International journal of molecular sciences
|March 13, 2025
PubMed
概括

腺相关病毒 (AAV) 载体对于体内基因治疗至关重要,克服血脑屏障以治疗神经疾病. 本综述涵盖了AAV生物学,工程和中枢神经系统疾病的临床应用.

关键词:
阿尔茨海默氏症是阿尔茨海默氏症的一种疾病.卡纳万病就是卡纳万病.亨廷顿病就是亨廷顿病.帕金森病是帕金森氏症的一种疾病.腺相关病毒的病毒.芳香的L-氨基酸脱碳酶缺乏症卡普西德工程 工程中枢神经系统中枢神经系统基因治疗的基因疗法

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