SITTER

Aleksandra Bieniaszewska1, Magdalena Sobieska2, Ewa Gajewska3

  • 1Department of Developmental Neurology, Poznan University of Medical Sciences, 60-355, Poznan, Poland. aleksandra.bieniaszewska.22@gmail.com.

Scientific reports
|March 29, 2025
PubMed
概括

脊柱肌肉缩 (SMA) 的新型疾病修饰疗法改善了5-20岁患者的运动功能. 虽然观察到功能上的收益,但结构上的变化,如联合合同,并没有持续地改善或对称地恶化.