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Updated: May 10, 2025

Lentiviral Vector-mediated Gene Therapy of Hepatocytes Ex Vivo for Autologous Transplantation in Swine
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基于基因治疗的脂肪性肝病基因疗法

Viktoriia Iakovleva1, Ype P de Jong1

  • 1Division of Gastroenterology and Hepatology, Weill Cornell Medicine, New York, NY 10021, USA.

Molecular therapy : the journal of the American Society of Gene Therapy
|April 21, 2025
PubMed
概括

基因疗法在治疗脂肪性肝病 (SLD) 方面表现有前途. 肝脏关键基因的遗传变异提供了治疗目标,目前正在进行的临床试验正在探索基因治疗以改善肝脏健康.

关键词:
在 AAV AAV AAV 中.这就是ALD.马什 (MASH) 是一个非常重要的产品.马斯尔德 马斯尔德是什么意思这是NAFLD.

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