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Updated: May 10, 2025

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新的药物可用于法布里病

Fernando Perretta, Gustavo Cabrera, Juan Politei

    Kidney & blood pressure research
    |April 27, 2025
    PubMed
    概括

    对法布里病 (FD) 的新疗法为患者提供了更好的选择. 新兴的疗法,如基质减少和基因疗法,对治疗这种遗传性疾病充满希望.

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