相关实验视频

Updated: May 9, 2025

Efficient and Scalable Production of Full-length Human Huntingtin Variants in Mammalian Cells using a Transient Expression System
10:52

Efficient and Scalable Production of Full-length Human Huntingtin Variants in Mammalian Cells using a Transient Expression System

Published on: December 10, 2021

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亨廷顿病临床试验更新:2025年3月

Mena Farag1, Sarah J Tabrizi1, Edward J Wild1

  • 1Huntington's Disease Centre, UCL Queen Square Institute of Neurology, London, UK.

Journal of Huntington's disease
|April 30, 2025
PubMed
概括

此更新涵盖正在进行的亨廷顿病临床试验,包括Alynlam的ALN-HTT02和Sage Therapeutics的SAGE-718 (dalzanemdor) 计划. 它还详细说明了uniQure的AMT-130的监管进展,并列出了所有当前的亨廷顿病试验.

关键词:
亨廷顿病就是亨廷顿病.临床试验是指临床试验中的临床试验.

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