在加拿大获取罕见病药物 (DRD):对省级DRD特定计划的全面审查
1School of Public Policy and Administration, Carleton University, 1125 Colonel By Drive, Ottawa, ON K1S 5B6, Canada.
Therapeutic advances in rare disease
|April 30, 2025
概括
加拿大加拿大加拿大加拿大加拿大加拿大
科学领域:
- 卫生政策 卫生政策
- 药品接入 药品接入 药品接入
- 罕见疾病 罕见疾病
背景情况:
- 由于省级药物审查流程,加拿大对罕见疾病 (DRDs) 药物的获取是分散的.
- 这种碎片化导致覆盖率差异,并导致罕见疾病 (RDs) 患者治疗机会延迟.
- 加拿大在采用DRD国家战略方面落后,尽管最近政府采取了一些举措.
研究的目的:
- 检查和比较加拿大针对DRD的省级药物计划.
- 识别DRD访问当前系统中的差距和低效率.
- 为制定统一的,基于证据的国家DRD政策提供信息.
主要方法:
- 对DRD特定计划 (DRD-SPs) 的政策文件进行定性文档审查.
- 分析的重点是安大略省,阿尔伯塔省,新不伦瑞克省,不列颠哥伦比亚省和萨斯喀彻温省的项目.
- 在2019年2月至2022年4月期间进行的研究.
主要成果:
- 阿尔伯塔省和新不伦瑞克省有活跃的DRD-SP;安大略省的框架已经终止.
- 萨斯喀彻温省缺乏DRD-SP,与一些迹象相反;BC的地位尚不清楚.
- 发现了一个缺乏协调的项目系统,缺乏明确的目标和绩效指标.
结论:
- 加拿大目前对DRD访问的做法是不协调和低效的.
- 统一的国家DRD政策对于一致和及时的患者接入至关重要.
- 纳入国内和国际洞察力可以加强加拿大的国家DRD战略.
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