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Updated: May 12, 2025

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杜维扎特 (givinostat):对于杜恩肌肉衰竭患者来说,这是一个新的希望

Nabiha Syed1, Zaib Un Nisa Mughal2, Abdul Haseeb2

  • 1Department of Medicine, Dow University of Health Sciences, Karachi, Pakistan.

Annals of medicine and surgery (2012)
|May 8, 2025
PubMed
概括

美国食品和药物管理局批准Duvyzat (givinostat) 用于杜申肌力发育不良症 (DMD),这是一种罕见的遗传性疾病. 这种基因组脱乙酶抑制剂提供了一种新的治疗选择,有可能改善DMD患者的肌肉功能.

关键词:
杜恩肌肉发育不良 (DMD)杜维扎特 (Duvyzat) 是一个给出一个统计数据.基因素脱乙酶抑制剂 基因素脱乙酶抑制剂

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